Gene therapy – personalised medicine in action

Marguerite V. Evans-Galea

“We all begin life as a single cell that divides and develops until we are a fully grown human being. Inside this cell, our DNA carries the complete set of instructions for this to happen. However, if your DNA sequence harbours an alteration — even a small, seemingly insignificant single-base sequence change — it can have detrimental consequences: inherited genetic disease …”